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    Rare Genetic Disease Stocks List

    Symbol Grade Name % Change
    BPMC C Blueprint Medicines Corporation 3.65
    ADVM D Adverum Biotechnologies, Inc. 1.58
    SYBX F Synlogic, Inc. 1.39
    INZY F Inozyme Pharma, Inc. 1.63
    BDTX F Black Diamond Therapeutics, Inc. 5.47
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    Related Industries: Biotechnology
    Related Stock Lists: Genetic Diseases Rare Genetic Diseases Cancer Disease Biology Biopharmaceutical Biotechnology Tyrosine Kinase Receptors Adverum Biotechnologies Black Diamond Cancer Treatment Cell Biology Cell Signaling Diabetes Diamond Enzymes Epidermal Growth Factor Receptor Fibroblast Growth Factor Receptor Gastrointestinal Gastrointestinal Stromal Tumor

    Related ETFs - A few ETFs which own one or more of the above listed Rare Genetic Disease stocks.

    Symbol Grade Name Weight
    CANC C Tema Oncology ETF 3.14
    PBE C PowerShares Dynamic Biotech & Genome 2.62
    LABD D Direxion Daily S&P Biotech Bear 3X Shares 2.16
    WDNA D WisdomTree BioRevolution Fund 2.12
    XBI B SPDR S&P Biotech ETF 1.51
    View all Rare Genetic Disease ETFs...
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    Compare LABD to WDNA Compare PBE to LABD Compare PBE to XBI

        Rare Genetic Disease Stocks Recent News

        Date Stock Title
        Nov 1 BPMC High Growth Tech Stocks to Watch in November 2024
        Nov 1 BPMC Blueprint Medicines Third Quarter 2024 Earnings: EPS Beats Expectations
        Nov 1 BDTX Black Diamond Therapeutics to Participate in Upcoming Investor Conferences
        Oct 31 BPMC BPMC Beats on Q3 Earnings and Sales, Raises '24 View, Stock Up
        Oct 31 BPMC Blueprint Medicines Corp (BPMC) Q3 2024 Earnings Call Highlights: Record AYVAKIT Revenue and ...
        Oct 31 BPMC Q3 2024 Blueprint Medicines Corp Earnings Call
        Oct 30 BPMC Blueprint Medicines Corporation (BPMC) Q3 2024 Earnings Call Transcript
        Oct 30 BPMC Blueprint Medicines (BPMC) Reports Q3 Loss, Tops Revenue Estimates
        Oct 30 BPMC Blueprint Medicines: Q3 Earnings Snapshot
        Oct 30 BPMC Blueprint Medicines beats Q3 top and bottom-line estimates
        Oct 30 BPMC Blueprint Medicines Reports Third Quarter 2024 Results and Raises AYVAKIT®/AYVAKYT® (avapritinib) Full Year Revenue Guidance
        Oct 29 BPMC Blueprint Medicines Q3 2024 Earnings Preview
        Oct 27 BPMC Blueprint Medicines Corporation (NASDAQ:BPMC): Are Analysts Optimistic?
        Related Industries: Biotechnology
        Related Stock Lists: Genetic Diseases Rare Genetic Diseases Cancer Disease Biology Biopharmaceutical Biotechnology Tyrosine Kinase Receptors Adverum Biotechnologies Black Diamond Cancer Treatment Cell Biology Cell Signaling Diabetes Diamond Enzymes Epidermal Growth Factor Receptor Fibroblast Growth Factor Receptor Gastrointestinal Gastrointestinal Stromal Tumor
        Rare Genetic Disease

        Rare genetic diseases are genetic disorders that are present in a very small percentage of the population. These diseases are caused by mutations in a single gene or a combination of genes, and can be inherited from a parent or occur spontaneously. Symptoms of rare genetic diseases can vary widely, and can range from mild to severe. Treatment options for rare genetic diseases are often limited, and may include medications, lifestyle changes, and surgery.

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