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    Rare Diseases Stocks List

    Symbol Grade Name % Change
    BLUE F bluebird bio, Inc. -2.08
    RLYB F Rallybio Corporaton 5.62
    BMRN F BioMarin Pharmaceutical Inc. 0.92
    AZTR F Azitra Inc. -0.36
    CNTG F Centogene N.V. 0.00
    GSK F GlaxoSmithKline PLC 0.63
    NGNE F Neurogene, Inc. -0.58
    XFOR F X4 Pharmaceuticals, Inc. 2.76
    LXEO F Lexeo Therapeutics, Inc. 1.47
    PASG F Passage Bio, Inc. 0.25
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    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biotechnology Biopharmaceutical Life Sciences Cancer Drug Discovery Hematology Medicine Molecule Product Organ Systems Pharmacy Syndromes Acid Alzheimer's Disease Anemia Angioedema Arcturus Therapeutics Ataxia Autoimmune Disease Biologics Bone

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    HELX D Franklin Genomic Advancements ETF 4.7
    SBIO C ALPS Medical Breakthroughs ETF 3.39
    BBP C BioShares Biotechnology Products Fund 2.97
    PSCH C PowerShares S&P SmallCap Health Care Portfolio 2.97
    JFWD B Jacob Funds Inc. Jacob Forward ETF 2.46
    View all Rare Diseases ETFs...
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    Compare BBP to PSCH Compare PSCH to JFWD Compare SBIO to JFWD

        Rare Diseases Stocks Recent News

        Date Stock Title
        Nov 20 GSK CDC warns of an imminent spike in COVID, flu cases
        Nov 20 XFOR Spotlight On 3 US Penny Stocks With At Least $60M Market Cap
        Nov 20 LXEO Here's Why We're Watching Lexeo Therapeutics' (NASDAQ:LXEO) Cash Burn Situation
        Nov 19 BMRN BioMarin Pharmaceutical Inc. (BMRN): Among the Best Genomics Stocks to Buy Right Now
        Nov 19 GSK GSK's Investigational Liver Disease Candidate Hits Primary Goal In Late-Stage Study To Treat Relentless Itch In Some Patients
        Nov 19 GSK GSK's Investigational Liver Disease Candidate Hits Primary Goal In Late-Stage Study To Treat Relentless Itch In Some Patients
        Nov 19 GSK GSK reports positive Phase 3 results for linerixibat in PBC itching
        Nov 19 NGNE Neurogene GAAP EPS of -$1.19 in-line
        Nov 18 NGNE Neurogene Reports Third Quarter 2024 Financial Results and Highlights Recent Updates
        Nov 18 NGNE How A Side Effect Has Wiped Out 73% Of Neurogene's Value In A Week
        Nov 18 NGNE Neurogene stock plunges 36% on NGN-401 study update
        Nov 18 GSK Medicus Pharma Ltd. Appoints Faisal Mehmud, MD, MRCP as Chief Medical Officer
        Nov 18 NGNE Neurogene Provides Update on NGN-401 Gene Therapy Clinical Trial for Rett Syndrome
        Nov 16 BMRN BioMarin Presents Real-World Evidence Further Supporting Safety and Efficacy of VOXZOGO® (vosoritide) in Children with Achondroplasia at the European Society for Paediatric Endocrinology (ESPE) Meeting 2024
        Nov 16 BLUE bluebird bio Third Quarter 2024 Earnings: EPS Beats Expectations, Revenues Lag
        Nov 15 GSK How analysts are reacting to RFK Jr. as Trump's HHS pick
        Nov 15 BLUE JP Morgan Downgrades Gene Therapy Focused Bluebird Bio, Cites Limited Funding Options
        Nov 15 GSK Stocks to Watch Friday: Applied Materials, Alibaba, Domino's, Novo Nordisk
        Nov 15 GSK Vaccine stocks drop on concerns about RFK Jr. heading HHS (update)
        Nov 15 BLUE bluebird bio extends selloff as BofA and J.P. Morgan cut after Q3 results
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Epidermolysis Bullosa Genodermatoses Disease Medicine Biotechnology Clinical Development Clinical Medicine Dermatology Gene Therapy Life Sciences Medical Genetics Organ Systems Acid Acute Pain Aesthetics Amphetamine Ataxia Attention Deficit Hyperactivity Disorder Biopharmaceutical Bone
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

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